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Pegvisomant

Phase 3

Acromegaly | Small molecule | Endocrine |Unity Biotechnology, Inc.|Last Updated: Nov 22, 2021

Success Probability
Approval Probability 71%
TA Base Rate26%
Adjusted LOA41%
ML RiskLOW_RISK
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Market & Valuation
rNPV $3.2B
Market Size $9.4B
Revenue Basis $1.6B
Competitors 6
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Trial Design
UNCONTROLLED
Total Trials1
Total Enrollment10
FDA Designations
No designations recorded
Clinical Trials (1)
NCT IDTitlePhaseStatusEnrollmentVelocityDesignStartCompletionLast UpdatedSitesCountries
NCT02952885Strict IGF-1 Control in AcromegalyPHASE3 COMPLETED 10Jul 27, 2017May 7, 2020Nov 22, 20215 Canada
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Study Endpoints
Primary Endpoints
Health Related Quality of Life (AcroQoL)
six months
Secondary Endpoints
Serum IGF-1 level
six months
Acromegaly Disease Activity Tool (ACRODAT)
six months
Patient-assessed Acromegaly Symptom Questionnaire
six months
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Study Design & Arms
AllocationNA
MaskingNONE
ModelSINGLE_GROUP
PurposeTREATMENT
Treatment Arms
ArmTypeDescription
PegvisomantEXPERIMENTALOpen-label, non-randomized single arm variable dose study of pegvisomant conducted in a real world setting.
Interventions
NameTypeDescription
PegvisomantDRUGStudy medications will be prescribed as per clinical practice with PEGV being added, or optimally dosed, at the Month 0 visit. Subjects who are naïve to PEGV should start their injections from 10 mg twice a week to 10 mg daily if used as combination therapy or 10 to 20 mg daily if used as monotherapy. Maximum dosing should not exceed 40mg/day. Dosing of PEGV can be adjusted as per clinical judgement to meet the normalization of IGF-1 levels (\<1.0 ULN) in increments of 5-10mg/day. In the event of a reduction in IGF-1 below the LLN, the dose of PEGV could be decreased by 5-10 mg/day.
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Eligibility Criteria
Age Range18 Years — N/A
SexALL
Healthy VolunteersNo
Study Sites5

Inclusion Criteria: * Adult patients (at least 18 years old) with confirmed acromegaly whose IGF-I levels are persistently but modestly (1.0 ULN \< \[IGF-1 serum level\] \< 1.5 ULN) elevated following medical therapy such as SSA, PEGV, cabergoline alone or in combination. Exclusion Criteria: 1. P...

Countries:Canada
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