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Intravitreal topotecan

Phase 2

Retinal Detachment Rhegmatogenous | Small molecule | Ophthalmology |Unity Biotechnology, Inc.|Last Updated: Mar 6, 2025

Success Probability
Approval Probability 71%
TA Base Rate26%
Adjusted LOA41%
ML RiskLOW_RISK
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Market & Valuation
rNPV $3.2B
Market Size $9.4B
Revenue Basis $1.6B
Competitors 6
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Trial Design
ACTIVE_CONTROLLEDBiomarker
Total Trials1
Total Enrollment394
FDA Designations
No designations recorded
Clinical Trials (1)
NCT IDTitlePhaseStatusEnrollmentVelocityDesignStartCompletionLast UpdatedSitesCountries
NCT06818721Intravitreal Topotecan for Prevention or Treatment of Proliferative Vitreoretinopathy in Retinal DetachmentPHASE2 NOT YET_RECRUITING 394Mar 1, 2025Apr 1, 2027Mar 6, 20252 Canada
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Study Endpoints
Primary Endpoints
Rate of recurrent rhegmatogenous retinal detachment secondary to proliferative vitreoretinopathy
6 months or last follow-up
Secondary Endpoints
Grade of proliferative vitreoretinopathy
6 months or last follow-up
Rate of primary retinal reattachment
6 months or last follow-up
Rate of final retinal reattachment
6 months or last follow-up
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Study Design & Arms
AllocationNON_RANDOMIZED
MaskingNONE
ModelPARALLEL
PurposePREVENTION
Treatment Arms
ArmTypeDescription
Intravitreal topotecan with retinal detachment surgeryEXPERIMENTALIntravitreal topotecan 8 µg/0.05mL, diluted in sterile saline and administered preoperatively, within one week prior to surgery, as well as one week postoperatively.
Retinal detachment surgeryACTIVE_COMPARATORHistorical control patients who previously received standard of care surgery for rhegmatogenous retinal detachment without intravitreal topotecan.
Interventions
NameTypeDescription
Intravitreal topotecanDRUGPatients who meet all inclusion criteria and none of the exclusion criteria will receive intravitreal topotecan (8 µg in 0.05 mL). The treatment will be administered within one week before retinal detachment surgery (pneumatic retinopexy, pars plana vitrectomy, and/or scleral buckling) and one week after surgery, for a total of two injections.
Retinal detachment surgeryPROCEDUREStandard retinal detachment surgery (pneumatic retinopexy, three-port pars plana vitrectomy, and/or scleral buckling).
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Eligibility Criteria
Age Range18 Years — N/A
SexALL
Healthy VolunteersNo
Study Sites2

Inclusion Criteria: 1. Patients aged 18 years and older 2. Patients who undergo pneumatic retinopexy, pars plana vitrectomy and/or scleral buckling for rhegmatogenous retinal detachment 3. Patients who are voluntarily able and willing to participate Patients undergoing combined phacoemulsification...

Countries:Canada
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Recent Changes (Last 90 Days)
LOWMay 26, 2026NCT06818721primaryCompletionDate: changed
LOWMay 24, 2026NCT06818721studyFirstPostDate: changed