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S 64315 and venetoclax

Phase 1

Acute Myeloid Leukaemia | Small molecule | Oncology |Tango Therapeutics, Inc.|Last Updated: Jun 6, 2024

Success Probability
Approval Probability 71%
TA Base Rate26%
Adjusted LOA41%
ML RiskLOW_RISK
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Market & Valuation
rNPV $3.2B
Market Size $9.4B
Revenue Basis $1.6B
Competitors 6
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Trial Design
CONTROLLEDDMCBiomarker
Total Trials2
Total Enrollment54
FDA Designations
No designations recorded
Clinical Trials (2)
NCT IDTitlePhaseStatusEnrollmentVelocityDesignStartCompletionLast UpdatedSitesCountries
NCT04629443Phase I/II Trial of S64315 Plus Azacitidine in Acute Myeloid LeukaemiaPHASE1 COMPLETED 17Feb 17, 2021Aug 25, 2023Jun 6, 20247 United States, Australia +2
NCT03672695Phase I Dose Escalation Study of Intravenously Administered S64315 in Combination With Orally Administered Venetoclax in Patients With Acute Myeloid Leukaemia.PHASE1 COMPLETED 37Nov 28, 2018May 30, 2023Feb 5, 20247 United States, Australia +1
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Study Endpoints
Primary Endpoints
Dose Limiting Toxicity (DLT) (Phase I - Dose Escalation)
Day -13 to Cycle 1 Day 28 (each cycle is 28 days)

Incidence of DLTs starting from the Lead-In Dose period to the end of the first cycle of treatment of S64315 in combination with azacitidine.

Number of Adverse Events (AEs) and Severe AEs (Phase I - Dose Escalation)
an average of 6 months

Incidence and severity of AEs according to NCI CTCAE v5.0

Number of Serious Adverse Event (SAEs) and Fatal SAEs (Phase I - Dose Escalation)
Day -13 up to 30 calendar days after the patient's last study visit (an average of 6 months)

Incidence and severity of SAEs according to NCI CTCAE v5.0

Number of Participants With Dose Interruptions (Phase I - Dose Escalation)
Through study completion, an average of 6 months
Number of Participants With Dose Reductions (Phase I - Dose Escalation)
Through study completion, an average of 6 months
Dose Intensity for S64315 (Phase I - Dose Escalation)
Through study completion, an average of 6 months
Dose Intensity for Azacitidine (Phase I - Dose Escalation)
Through study completion, an average of 6 months
Incidence of Dose Limiting Toxicity (DLTs)
At the end of cycle 1 (each cycle is 21 or 28 days).
Incidence and severity of AEs
Through study completion, an average of 6 months.
Incidence and severity of SAEs
Through study completion, an average of 6 months.
Number of participants with dose interruptions "will be measured and reported in the Outcome Measure results data table.
Through study completion, an average of 6 months.
Number of participants with dose reductions "will be measured and reported in the Outcome Measure results data table.
Through study completion, an average of 6 months.
Dose intensity
Through study completion, an average of 6 months.
Secondary Endpoints
Assess Anti-leukemic Activity of S64315 in Combination With Azacitidine (Phase I - Dose Escalation)
Through study completion, an average of 6 months
Assess Anti-leukemic Activity of S64315 in Combinaison With Azacitidine (Phase I - Dose Escalation)
Through study completion, an average of 6 months
Pharmacokinetic Profile of S64315 Administered in Combination With Azacitidine in Plasma: Area Under the Curve (AUC) (Phase I - Dose Escalation)
At Cycle 1 Day 2 and Cycle 1 Day 9 (each cycle is 28 days)
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Study Design & Arms
AllocationNA
MaskingNONE
ModelSINGLE_GROUP
PurposeTREATMENT
Treatment Arms
ArmTypeDescription
S64315 (also referred as MIK665) with azacitidineEXPERIMENTAL -
Initial Schedule - S64315 low dose and venetoclax high dose administered in combinationEXPERIMENTAL -
Initial Schedule - S64315 medium dose and venetoclax low dose administered in combinationEXPERIMENTAL -
Initial Schedule - S64315 medium dose and venetoclax medium dose administered in combinationEXPERIMENTAL -
Initial Schedule - S64315 medium dose and venetoclax high dose administered in combinationEXPERIMENTAL -
Initial Schedule - S64315 high dose and venetoclax medium dose administered in combinationEXPERIMENTAL -
Alternative Schedule - Venetoclax medium dose administered with no S64315EXPERIMENTAL -
Alternative Schedule - S64315 medium dose and venetoclax medium dose administered in combinationEXPERIMENTAL -
Alternative Schedule - S64315 high dose and venetoclax low dose administered in combinationEXPERIMENTAL -
Interventions
NameTypeDescription
S 64315 (also referred as MIK665) and azacitidineDRUGThe combination treatment at the planned doses may be preceded by a 2-week Lead-In Dose period of S64315 (fixed dose) administered via intravenous (IV) infusion over at least 2 hours. During the combination treatment period S64315 will be administered according to a dose escalation scheme starting at 50 mg up to 250 mg might be explored. The schedule will be a 21-day cycle with a weekly regimen for S64315 and a daily regimen of azacitidine administered at 75 mg/m² via subcutaneous (SC) injection for 7 days from D1 to D7 of each cycle followed by a rest period of 21 days.
S 64315 (also referred as MIK665) and venetoclaxCOMBINATION_PRODUCTThe treatment combination period can only begin after the planned dose of venetoclax is reached. Depending on the administration dosing schedule, the combination treatment at the planned doses may be preceded by a 2-week Lead-In Dose period of S64315 (fixed dose) during which the patient continues to receive venetoclax daily. Once the planned dose of both drugs is reached the schedule will be a 21-day cycle with a weekly regimen for S64315 and a daily regimen for venetoclax. S64315 should be administered 2 to 4 hours after venetoclax intake, via IV infusion. The dose escalation will start at 50 mg once a week and doses up to 250 mg once a week might be explored. Venetoclax will be administered orally once a day. The dose escalation will start at 100 mg daily and doses up to 600 mg daily might be explored. Venetoclax must be taken with a meal (ideally during breakfast) in order to avoid reduced efficacy.
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Eligibility Criteria
Age Range18 Years — N/A
SexALL
Healthy VolunteersNo
Study Sites7

Inclusion Criteria: 1. Patients aged ≥ 18 years 2. Patients with cytologically confirmed and documented de novo, secondary or therapy-related AML as defined by World Health Organization 2016 classification (Arber, 2016) excluding acute promyelocytic leukaemia (APL, French American-British M3 classi...

Countries:United StatesAustraliaFranceSpain
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