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Ivosidenib + azacitidine

Phase 2

Acute Myeloid Leukemia | Small molecule | Oncology |Tango Therapeutics, Inc.|Last Updated: Mar 11, 2026

Success Probability
Approval Probability 71%
TA Base Rate26%
Adjusted LOA41%
ML RiskLOW_RISK
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Market & Valuation
rNPV $3.2B
Market Size $9.4B
Revenue Basis $1.6B
Competitors 6
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Trial Design
UNCONTROLLEDDMCBiomarker
Total Trials2
Total Enrollment105
FDA Designations
No designations recorded
Clinical Trials (2)
NCT IDTitlePhaseStatusEnrollmentVelocityDesignStartCompletionLast UpdatedSitesCountries
NCT07463768Study Evaluating the Efficacy and Safety of the Addition of Ivosidenib to Oral Azacitidine (Onureg®) in Patients Over 55 With Acute Myeloid Leukemia (AML) and IDH1 Mutation, in Complete Remission After Intensive Chemotherapy.PHASE2 NOT YET_RECRUITING 60Sep 1, 2026Sep 1, 2030Mar 11, 202620 France
NCT07392242A Study of the Combination of Ivosidenib, Azacitidine, and Venetoclax Followed by Ivosidenib Alone in People With Acute Myeloid LeukemiaPHASE2 RECRUITING 45Jan 27, 2026Jan 1, 2028Mar 6, 20267 United States
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Study Endpoints
Primary Endpoints
RFS 24 months
24 months

relapse-free-survival (RFS) at 24 months in patients receiving oral azacitidine with ivosidenib

Event free survival
12 months

Event-free survival is defined as the time between date of treatment start to treatment failure (failure to achieve complete remission or \<5% bone marrow blasts), confirmed relapse or death.

Secondary Endpoints
RFS 12 months
12 months
Overall survival
24 months
EFS MRD neg
24 months
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Study Design & Arms
AllocationNA
MaskingNONE
ModelSINGLE_GROUP
PurposeTREATMENT
Treatment Arms
ArmTypeDescription
ivosidenib + Oral azacitidineEXPERIMENTALcf intervention
Ivosidenib, Azacitidine, and Venetoclax Followed by Ivosidenib AloneEXPERIMENTALPatients will be initially treated with 7 days of azacitidine (IV or SC per institutional preference, 14 days of venetoclax and 14 days of Ivosidenib daily, days 15 through 28 for cycle 1, then days 1 through 28 for each cycle thereafter).
Interventions
NameTypeDescription
Ivosidenib + oral azacitidineDRUGSubjects will be administered treatment over 28-day cycles until progression or another reason (unacceptable toxicity, patient choice to discontinue study treatment, sponsor decision, HSCT at any time, patients who require the use of any of the excluded therapies). The treatment is the association of ivosidenib with oral azacitidine. * The investigational medicinal product is ivosidenib. Two tablets (500 mg) will be administered as a single dose, once daily, during 28 days-cycles until discontinuation. * The auxiliary treatment is oral azacitidine. Oral AZA 300 mg will be given once-daily for 14 days of repeated 28-day treatment cycles. For all patients, oral AZA will be interrupted systematically after day 14 of each 28-days cycle.
IvosidenibDRUGIvosidenib ( days 15 through 28 for cycle 1, then days 1 through 28 for each cycle thereafter)
AzacitidineDRUGAzacitidine (IV or SC per institutional preference, days 1 through 7)
VenetoclaxDRUGVenetoclax (days 1 through 14)
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Eligibility Criteria
Age Range55 Years — N/A
SexALL
Healthy VolunteersNo
Study Sites20

Inclusion Criteria: 1. Male or female ≥ 55 years of age at the time of signing informed consent 2. Patients with confirmation of newly diagnosed AML by 2022 WHO criteria 3. Presence of IDH1 R132 mutation at AML diagnosis 4. Achievement CR or CRi following induction therapy by intensive chemotherapy...

Countries:FranceUnited States
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Recent Changes (Last 90 Days)
LOWMay 24, 2026NCT07392242studyFirstPostDate: changed
LOWMay 24, 2026NCT07463768studyFirstPostDate: changed