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Arm NaI-IRI + 5-FU + Leucovorin

Phase 2

Adenocarcinoma Metastatic | Small molecule | Oncology |Tango Therapeutics, Inc.|Last Updated: Oct 1, 2025

Success Probability
Approval Probability 71%
TA Base Rate26%
Adjusted LOA41%
ML RiskLOW_RISK
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Market & Valuation
rNPV $3.2B
Market Size $9.4B
Revenue Basis $1.6B
Competitors 6
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Trial Design
RandomizedCONTROLLEDBiomarker
Total Trials1
Total Enrollment93
FDA Designations
No designations recorded
Clinical Trials (1)
NCT IDTitlePhaseStatusEnrollmentVelocityDesignStartCompletionLast UpdatedSitesCountries
NCT03044587Nal-IRI With 5-fluorouracil (5-FU) and Leucovorin or Gemcitabine Plus Cisplatin in Advanced Biliary-tract CancerPHASE2 COMPLETED 93Jan 24, 2018Jan 31, 2025Oct 1, 20251 Germany
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Study Endpoints
Primary Endpoints
Progression-free survival [PFS]
approx. 25 months
Secondary Endpoints
Overall progression free survival according to RECIST 1.1
approx. 54 months
3-years overall survival
approx. 36 months
Disease control rate according to RECIST 1.1
approx. 54 months
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Study Design & Arms
AllocationRANDOMIZED
MaskingNONE
ModelPARALLEL
PurposeTREATMENT
Treatment Arms
ArmTypeDescription
Arm NaI-IRI + 5-FU + Leucovorin (Arm A)EXPERIMENTALNal-IRI \[Irinotecan liposome\], 5-FU \[5-Fluorouracil\], Leucovorin Cycle q2w
Arm Cisplatin + Gemcitabine (Arm B, standard of care)OTHERCisplatin, Gemcitabine Cycle q3w
Interventions
NameTypeDescription
Arm NaI-IRI + 5-FU + Leucovorin (Arm A)DRUGNal-IRI (80 mg/m2 as a 1.5 hour infusion), 5-FU (2400 mg/m2 as 46 hour infusion) and Leucovorin (400 mg/m2 as 0.5 hour infusion) Cycle q2w
Arm Cisplatin + Gemcitabine (Arm B)DRUGCisplatin (25 mg/m2 as 1 hour infusion on D1, D8) and Gemcitabine (1000 mg/m2 as 0.5 hour infusion on D1, D8) Cycle q3w
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Eligibility Criteria
Age Range18 Years — N/A
SexALL
Healthy VolunteersNo
Study Sites1

Inclusion Criteria: 1. Written informed consent incl. participation in translational research and any locally-required authorization (EU Data Privacy Directive in the EU) obtained from the subject prior to performing any protocol-related procedures, including screening evaluations 2. Age ≥ 18 years...

Countries:Germany
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