Recent Updates
Recently added Catalysts

bsi-201 + topotecan

Phase 1

Tumors | Small molecule | Oncology |Sanofi|Last Updated: Jun 10, 2016

Success Probability
Approval Probability 71%
TA Base Rate26%
Adjusted LOA41%
ML RiskLOW_RISK
Premium
Market & Valuation
rNPV $3.2B
Market Size $9.4B
Revenue Basis $1.6B
Competitors 6
Premium
Trial Design
CONTROLLEDBiomarker
Total Trials2
Total Enrollment195
FDA Designations
No designations recorded
Clinical Trials (2)
NCT IDTitlePhaseStatusEnrollmentVelocityDesignStartCompletionLast UpdatedSitesCountries
NCT00422682A Study Evaluating BSI-201 in Combination With Chemotherapeutic Regimens in Subjects With Advanced Solid TumorsPHASE1 COMPLETED 136Jan 1, 2007Oct 1, 2012Jun 10, 20166 United States
NCT00298675Phase 1/1b Dose Escalation Study Evaluating BSI-201 as a Single Agent and in Combination With Irinotecan in Subjects With Advanced Solid TumorsPHASE1 COMPLETED 59Mar 1, 2006May 1, 2011Aug 2, 20123 United States
Unlock Drug Trial Details
Study Endpoints
Primary Endpoints
safety and efficacy
ongoing
Response rate (CR + PR)
every 2 cycles
Maximum tolerated dose
After one cycle
Secondary Endpoints
Clinical Response
8 months
Unlock Study Endpoints
Study Design & Arms
AllocationNON_RANDOMIZED
MaskingNONE
ModelPARALLEL
PurposeTREATMENT
Treatment Arms
ArmTypeDescription
1EXPERIMENTALBSI-201 + topotecan
2EXPERIMENTALBSI-201 + temozolomide
3EXPERIMENTALbsi-201 + gemcitabine
4EXPERIMENTALbsi-201 + carboplatin/paclitaxel
IniparibEXPERIMENTAL -
Iniparib/irinotecanEXPERIMENTAL -
Interventions
NameTypeDescription
bsi-201 + topotecanDRUG21 day cycle
bsi-201 + temozolomideDRUG28 day cycle
bsi-201 + gemcitabineDRUG28 day cycle
bsi-201 + carboplatin/paclitaxelDRUG21 day cycle
BSI-201 (iniparib)DRUGBSI-201 administered intravenously (IV), 2x weekly
irinotecanDRUGIrinotecan administered weekly, IV.
Unlock Study Design Details
Eligibility Criteria
Age Range18 Years — N/A
SexALL
Healthy VolunteersNo
Study Sites6

Inclusion Criteria: * ≥ 18 years old with a histologically or cytologically documented, advanced solid tumor * Eastern Cooperative Oncology Group (ECOG) performance status of ≤ 1 * Absolute neutrophil count (ANC) ≥ 1.5 x 10\^9/L (without granulocyte colony-stimulating factor \[G-CSF\] support withi...

Countries:United States
Unlock Eligibility Criteria
Competitive Landscape -Brain Tumors 139 trials
CompanyTickerTrialsLead PhaseDrugs
NovoCure Ltd.NVCR5PHASE3Temozolomide, Pembrolizumab, Poly-ICLC, Peptides, Concurrent Optune and RT followed by Optune System alone
Jazz Pharmaceuticals Public Limited CompanyJAZZ4PHASE3Dordaviprone, Everolimus, ONC201, JZP3507, ONC206
Day One Biopharmaceuticals, Inc.DAWN2PHASE3Tovorafenib, Chemotherapeutic Agent
Nuvation Bio, Inc. Class ANUVB1PHASE3safusidenib
Tango Therapeutics, Inc.TNGX3PHASE3Vorasidenib, Temozolomide, TNG456, abemaciclib
Telix Pharmaceuticals Limited Sponsored ADRTLX2PHASE3TLX-101-Tx + Lomustine, 131I-IPA
Eli Lilly and CompanyLLY3PHASE2Abemaciclib, Temozolomide, LY3410738, Gemcitabine, Cisplatin
Pfizer Inc.PFE3PHASE2Palbociclib, Temozolomide, Irinotecan, Topotecan, Cyclophosphamide
Novartis AG Sponsored ADRNVS3PHASE2Dabrafenib, Trametinib, Lu-NeoB, Ga-NeoB, Lu-DOTA-TATE
NeOnc Technologies Holdings, Inc.NTHI4PHASE2NEO100, NEO212, Ipilimumab, Pembrolizumab, Nivolumab
Exelixis, Inc.EXEL2PHASE2Zanzalintinib, Cabozantinib
CNS Pharmaceuticals, Inc.CNSP1PHASE2Berubicin, Lomustine
Black Diamond Therapeutics, Inc.BDTX1PHASE2silevertinib in combination with temozolomide, temozolomide
Actuate Therapeutics, Inc.ACTU1PHASE29-ING-41, Gemcitabine - 21 day cycle, Doxorubicin., Lomustine, Carboplatin.
Rigel Pharmaceuticals, Inc.RIGL1PHASE2Olutasidenib + TMZ
Apollomics Inc. Class AAPLM1PHASE2APL-101
ImmunityBio IncIBRX1PHASE2Bevacizumab, PD-L1 t-haNK, N-803
Cooper Companies, Inc.COO1PHASE2Pre-radiation temozolomide.
Incyte CorporationINCY1PHASE2Ruxolitinib, Temozolomide
AstraZeneca PLCAZN2PHASE1AZD1390, Olaparib, Durvalumab, Physicians Choice systemic chemotherapy
Unlock Competitive Intelligence