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fresolimumab

Phase 2

Primary Focal Segmental Glomerulosclerosis | Small molecule | Other |Sanofi|Last Updated: Aug 26, 2015

Success Probability
Approval Probability 71%
TA Base Rate26%
Adjusted LOA41%
ML RiskLOW_RISK
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Market & Valuation
rNPV $3.2B
Market Size $9.4B
Revenue Basis $1.6B
Competitors 6
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Trial Design
RandomizedDouble-BlindPLACEBO_CONTROLLEDDMCBiomarker
Total Trials1
Total Enrollment36
FDA Designations
No designations recorded
Clinical Trials (1)
NCT IDTitlePhaseStatusEnrollmentVelocityDesignStartCompletionLast UpdatedSitesCountries
NCT01665391A Study of Fresolimumab in Patients With Steroid-Resistant Primary Focal Segmental Glomerulosclerosis (FSGS)PHASE2 COMPLETED 36Aug 1, 2012Nov 1, 2014Aug 26, 201532 United States, Brazil +3
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Study Endpoints
Primary Endpoints
Percentage of patients achieving partial remission (PR) or complete remission (CR) in urinary protein: creatinine ratio (Up/c ratio)
Up to Day 112
Number of patients reporting adverse events (AEs), serious adverse events (SAEs), and medical events of interest (MEOIs)
Up to Day 112
Secondary Endpoints
Percentage of patients achieving CR in Up/c ratio
Up to Day 112
Percentage of patients achieving PR in Up/c ratio
Up to Day 112
Change from baseline in Up/c ratio and urinary protein excretion rate
Up to Day 112
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Study Design & Arms
AllocationRANDOMIZED
MaskingDOUBLE
ModelPARALLEL
PurposeTREATMENT
Treatment Arms
ArmTypeDescription
fresolimumab 1 mg/kg total body weightEXPERIMENTAL -
fresolimumab 4 mg/kg total body weightEXPERIMENTAL -
PlaceboPLACEBO_COMPARATOR -
Interventions
NameTypeDescription
fresolimumabDRUG1 mg/kg total body weight administered intravenous (IV)
PlaceboDRUGPlacebo administered to match active treatment group
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Eligibility Criteria
Age Range18 Years — N/A
SexALL
Healthy VolunteersNo
Study Sites32

Inclusion Criteria: * The patient's renal biopsy is consistent with the diagnosis of primary Focal Segmental Glomerulosclerosis (FSGS) including all histological subtypes. * The patient has an eGFR ≥ 30 mL/min/1.73 m2 * The patient has a urinary total protein:creatinine ratio ≥ 3 mg protein/mg crea...

Countries:United StatesBrazilGermanyItalySpain
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