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Standard First-Line Therapy

Phase 2

Unresectable Colorectal Cancer | Small molecule | Oncology |Rocket Pharmaceuticals, Inc.|Last Updated: Apr 3, 2026

Success Probability
Approval Probability 71%
TA Base Rate26%
Adjusted LOA41%
ML RiskLOW_RISK
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Market & Valuation
rNPV $3.2B
Market Size $9.4B
Revenue Basis $1.6B
Competitors 6
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Trial Design
RandomizedACTIVE_CONTROLLEDDMCBiomarker
Total Trials1
Total Enrollment220
FDA Designations
No designations recorded
Clinical Trials (1)
NCT IDTitlePhaseStatusEnrollmentVelocityDesignStartCompletionLast UpdatedSitesCountries
NCT07509398FMT Combined With Standard First-Line Therapy in Initially Unresectable Colorectal CancerPHASE2 NOT YET_RECRUITING 220Apr 1, 2026Dec 1, 2031Apr 3, 2026 -
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Study Endpoints
Primary Endpoints
Objective Response Rate
Up to 12 months (from randomization to best overall response assessment)
Secondary Endpoints
Conversion Resection Rate (R0)
Up to 12 months
Progression-Free Survival (PFS)
Up to 12 months
Disease Control Rate
Up to 12 months
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Study Design & Arms
AllocationRANDOMIZED
MaskingNONE
ModelPARALLEL
PurposeTREATMENT
Treatment Arms
ArmTypeDescription
Standard First-Line TherapyACTIVE_COMPARATORPatients receive investigator's choice of standard first-line systemic therapy for initially unresectable colorectal cancer (e.g., chemotherapy ± targeted therapy or anti-angiogenic agents according to CSCO/NCCN guidelines and RAS status).
FMT Combined with Standard First-Line TherapyEXPERIMENTALPatients receive fecal microbiota transplantation (FMT) in addition to the same standard first-line systemic therapy as in the control arm. FMT is administered according to the study protocol (donor-screened, prepared under GMP/P2 conditions, capsule delivery).
Interventions
NameTypeDescription
Standard First-Line TherapyDRUGInvestigator's choice of standard first-line systemic therapy for initially unresectable colorectal cancer, including chemotherapy (e.g., FOLFOX, FOLFIRI, CAPOX) with or without targeted therapy or anti-angiogenic agents (e.g., cetuximab, panitumumab for RAS wild-type; bevacizumab for others), according to CSCO/NCCN guidelines and RAS mutation status.
FMT Combined with Standard First-Line TherapyCOMBINATION_PRODUCTFecal microbiota transplantation using donor stool from healthy screened donors. Prepared under P2/GMP conditions as capsules or suspension. Administered in addition to standard therapy per study protocol (induction phase followed by maintenance).
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Eligibility Criteria
Age Range18 Years — 75 Years
SexALL
Healthy VolunteersNo

Inclusion Criteria: * (1) Subjects must volunteer to participate in this study, sign the informed consent form (ICF), and demonstrate good compliance. (2) Patients aged 18 to 75 years (inclusive). (3) Meet the defined criteria for initially unresectable advanced metastatic colorectal cancer (mCR...

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Recent Changes (Last 90 Days)
LOWMay 24, 2026NCT07509398studyFirstPostDate: changed