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BPS804 /Kg

Phase 2

Osteopenia | Small molecule | Endocrine |Ultragenyx Pharmaceutical Inc.|Last Updated: Sep 15, 2022

Success Probability
Approval Probability 71%
TA Base Rate26%
Adjusted LOA41%
ML RiskLOW_RISK
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Market & Valuation
rNPV $3.2B
Market Size $9.4B
Revenue Basis $1.6B
Competitors 6
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Trial Design
RandomizedDouble-BlindPLACEBO_CONTROLLEDBiomarker
Total Trials1
Total Enrollment44
FDA Designations
No designations recorded
Clinical Trials (1)
NCT IDTitlePhaseStatusEnrollmentVelocityDesignStartCompletionLast UpdatedSitesCountries
NCT01406548Safety and Efficacy of Multiple Dosing Regimens of BPS804 in Post Menopausal Women With Low Bone Mineral DensityPHASE2 COMPLETED 44Jul 1, 2011Oct 1, 2013Sep 15, 20225 United States
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Study Endpoints
Primary Endpoints
Change from baseline to month 9 in bone mineral density at the lumbar spine for the individual BPS804 groups and pooled placebo arms.
9 months
The number (percent) of subjects experiencing adverse events or serious adverse events
9 months
Secondary Endpoints
Change from baseline during 9 months of serological bone biomarkers for the individual BPS804 groups and pooled placebo arms.
9 months
Characterization of the PK profile of BPS804: area under the plasma concentration-time curve (AUC)
260 days
Characterization of the PK profile of BPS804: time to reach the maximum Characterization of the PK profile of BPS804: maximum plasma concentration (Cmax)
260 days
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Study Design & Arms
AllocationRANDOMIZED
MaskingQUADRUPLE
ModelPARALLEL
PurposeTREATMENT
Treatment Arms
ArmTypeDescription
BPS804 dosing frequency 1EXPERIMENTALSubjects dosed 20mg/Kg BPS804 monthly
placebo dosing frequency 1PLACEBO_COMPARATORSubjects dosed with matching placebo to 20mg/Kg BPS804 monthly
BPS804 dosing frequency 2EXPERIMENTALSubjects dosed with 20mg/Kg BPS804 quarterly
placebo dosing frequency 2PLACEBO_COMPARATORSubjects dosed with matching placebo to 20mg/Kg BPS804 every 3 months
BPS804 dosing frequency 3EXPERIMENTALSubjects dosed with 20mg/Kg BPS804 weekly
Placebo dosing frequency 3PLACEBO_COMPARATORSubjects dosed with matching placebo to 20mg/Kg BPS804 weekly
Interventions
NameTypeDescription
BPS804 20mg/KgDRUG -
Placebo to 20mg/Kg BPS804DRUG -
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Eligibility Criteria
Age Range45 Years — 85 Years
SexFEMALE
Healthy VolunteersNo
Study Sites5

Inclusion Criteria: * Postmenopausal women (natural or surgically induced menopause) * Low bone mineral density (BMD), as defined by a T score or equivalent BMD absolute value (g/cm2) for lumbar spine of between -2.0 and -3.5, inclusive * Body mass index (BMI) must be within the range of 18 to 35kg...

Countries:United States
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