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PRGN-2012 - Phase I; Dose Level 1

Phase 1

Recurrent Respiratory Papillomatosis | Small molecule | Other |Precigen, Inc.|Last Updated: Jun 11, 2025

Success Probability
Approval Probability 71%
TA Base Rate26%
Adjusted LOA41%
ML RiskLOW_RISK
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Market & Valuation
rNPV $3.2B
Market Size $9.4B
Revenue Basis $1.6B
Competitors 6
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Trial Design
CONTROLLEDBiomarker
Total Trials1
Total Enrollment38
FDA Designations
BREAKTHROUGH_THERAPYORPHAN_DRUG
Clinical Trials (1)
NCT IDTitlePhaseStatusEnrollmentVelocityDesignStartCompletionLast UpdatedSitesCountries
NCT04724980Adjuvant PRGN-2012 in Adult Patients With Recurrent Respiratory PapillomatosisPHASE1 ACTIVE NOT_RECRUITING 38Mar 16, 2021Jun 5, 2026Jun 11, 20251 United States
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Study Endpoints
Primary Endpoints
Determine the percentage of subjects with a complete response following treatment with PRGN-2012
1 year

A complete response is defined as no requirement for surgical intervention in the 12 months after treatment

Determine the incidence of dose limiting toxicities to evaluate safety and identify RP2D of PRGN-2012
28 days

The incidence of dose limiting toxicities in Phase 1 will be reported per dose level. The dose level at which less than or equal to 1 out of 6 patients experience DLT will be identified as a RP2D.

Secondary Endpoints
Safety of PRGN 2012 at RP2D
1 year
Immune Responses
1 year
Change in RRP Staging Assessment Scores Over Time
1 year
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Study Design & Arms
AllocationNON_RANDOMIZED
MaskingNONE
ModelSEQUENTIAL
PurposeTREATMENT
Treatment Arms
ArmTypeDescription
Phase I; Dose Level 1EXPERIMENTALA standard dose escalation design was used to evaluate PRGN-2012 at a dose level of 1 × 10\^11
Phase I; Dose Level 2EXPERIMENTALA standard dose escalation design was used to evaluate PRGN-2012 at a dose level of 5 × 10\^11
Phase II; Dose Level 2EXPERIMENTALA dose of 5 x 10\^11 PU was established as the RP2D, and the Phase 2 portion was implemented. The Phase 2 portion is designed as a dose expansion study, where patients were treated at the RP2D to evaluate the safety and efficacy of PRGN-2012.
Interventions
NameTypeDescription
PRGN-2012 - Phase I; Dose Level 1DRUGIn Phase 1, dose level 1 of the clinical trial, PRGN-2012 is administered at 1 × 10\^11 particle units as adjuvant therapy prior to standard debulking surgery.
PRGN-2012 - Phase I; Dose Level 2DRUGIn Phase 1, dose level 2 of the clinical trial, PRGN-2012 is administered at 5 × 10\^11 particle units as adjuvant therapy prior to standard debulking surgery.
PRGN-2012 - Phase II; Dose Level 2DRUGThe Phase 2 portion is designed as a dose expansion study where patients are treated at the RP2D of 5 x 10\^11 PU.
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Eligibility Criteria
Age Range18 Years — N/A
SexALL
Healthy VolunteersNo
Study Sites1

INCLUSION CRITERIA: * Age 18 years and older * Clinical diagnosis of RRP * Histological diagnosis of papilloma confirmed by pathology report from a CLIA-certified (or comparable) laboratory * Presence of laryngotracheal papillomas with or without pulmonary RRP * A history of 3 or more interv...

Countries:United States
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Recent Changes (Last 90 Days)
LOWMay 26, 2026NCT04724980primaryCompletionDate: changed
LOWMay 24, 2026NCT04724980studyFirstPostDate: changed