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Aromatase Inhibitor

Phase 3

Idiopathic Short Stature | Small molecule | Other |Pfizer, Inc.|Last Updated: Aug 7, 2018

Success Probability
Approval Probability 71%
TA Base Rate26%
Adjusted LOA41%
ML RiskLOW_RISK
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Market & Valuation
rNPV $3.2B
Market Size $9.4B
Revenue Basis $1.6B
Competitors 6
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Trial Design
RandomizedACTIVE_CONTROLLEDDMCBiomarker
Total Trials1
Total Enrollment76
FDA Designations
No designations recorded
Clinical Trials (1)
NCT IDTitlePhaseStatusEnrollmentVelocityDesignStartCompletionLast UpdatedSitesCountries
NCT01248416Aromatase Inhibitors, Alone And In Combination With Growth Hormone In Adolescent Boys With Idiopathic Short StaturePHASE3 COMPLETED 76Nov 1, 2010Sep 1, 2016Aug 7, 20184 United States, Chile
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Study Endpoints
Primary Endpoints
Change in Height
0 to 24 months

Differences in height gains

Change in Predicted Height
0 to 24 months

Primary efficacy end point: change in predicted height (cm) from baseline at 24 months based on change in bone age (years)

Secondary Endpoints
Change in Bone Density z Score Adjusted for Height
0 to 24 months
Change in Lean Body Mass
0 to 24 months
Change in Body Mass Index
0 to 24 months
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Study Design & Arms
AllocationRANDOMIZED
MaskingNONE
ModelPARALLEL
PurposeTREATMENT
Treatment Arms
ArmTypeDescription
Aromatase InhibitorACTIVE_COMPARATORAnastrozole 1mg or Letrozole 2.5mg daily orally for 2 to 3 years
Growth HormoneACTIVE_COMPARATORSomatropin 0.3mg/kg/week divided daily subcutaneously for 2 to 3 years
Aromatase Inhibitor and Growth HormoneACTIVE_COMPARATORAnastrozole 1mg or Letrozole 2.5mg orally daily for 2 to 3 years and Somatropin 0.3mg/kg/week divided daily subcutaneously for 2 to 3 years
Interventions
NameTypeDescription
Aromatase InhibitorDRUG -
Growth HormoneDRUG -
Aromatase Inhibitor and Growth HormoneDRUG -
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Eligibility Criteria
Age Range12 Years — 18 Years
SexMALE
Healthy VolunteersNo
Study Sites4

Inclusion Criteria: * Males: Ages: 12 - less than 18 years. * Bone age less than 14 ½ years at study initiation. * Presence of puberty. * Idiopathic short stature will be defined as a short child equal or less than -2SD for height, with normal GH responses to stimuli (\> or = 5ng/ml to at least 2 s...

Countries:United StatesChile
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