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ST571 + BYL719

Phase 1

3rd Line GIST | Small molecule | Other |Novartis AG|Last Updated: Dec 21, 2020

Success Probability
Approval Probability 71%
TA Base Rate26%
Adjusted LOA41%
ML RiskLOW_RISK
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Market & Valuation
rNPV $3.2B
Market Size $9.4B
Revenue Basis $1.6B
Competitors 6
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Trial Design
UNCONTROLLEDBiomarker
Total Trials1
Total Enrollment56
FDA Designations
No designations recorded
Clinical Trials (1)
NCT IDTitlePhaseStatusEnrollmentVelocityDesignStartCompletionLast UpdatedSitesCountries
NCT01735968A Dose-finding Study of a Combination of Imatinib and BYL719 in the Treatment of 3rd Line GIST PatientsPHASE1 COMPLETED 56Feb 27, 2013Oct 19, 2018Dec 21, 202011 United States, Belgium +6
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Study Endpoints
Primary Endpoints
Frequency of dose limiting toxicities (DLTs)
28 days (1st cycle)

Dose limiting toxicity (DLT) will be assessed using Common Terminology Criteria for Adverse Events (CTCAE) (v4.0.3), unless otherwise specified in the protocol.

Characteristics of dose limiting toxicities (DLTs)
28 days (1st cycle)

Dose limiting toxicity (DLT) will be assessed using Common Terminology Criteria for Adverse Events (CTCAE) (v4.0.3), unless otherwise specified in the protocol.

Secondary Endpoints
Frequency and characteristics of DLTs
28 days (1st cycle)
Imatinib and BYL719 plasma concentrations vs time profile
28 days (1st cycle)
Clinical benefit rate (CBR)
28 days (1st cycle)
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Study Design & Arms
AllocationNA
MaskingNONE
ModelSINGLE_GROUP
PurposeTREATMENT
Treatment Arms
ArmTypeDescription
STI571 (imatinib mesylate) and BYL719EXPERIMENTALThe study will comprise of 2 parts. A dose escalation and a dose expansion part. All patients in the dose escalation part will have a pharmacokinetic (PK) run-in period of 7 days receiving imatinib monotherapy. Patients will receive increasing doses of BYL719 (200, 300, 400 mg) in combination with 400mg imatinib daily until maximum tolerated dose (MTD) and rapid phase 2 dose (RP2D) is determined. Approximately 35 patients will enter the expansion phase.
Interventions
NameTypeDescription
ST571 + BYL719DRUGEvaluable patients must meet the minimum treatment and safety evaluation requirements of the study. Patients will be treated until they experience progression of disease, withdraw consent, or experience unacceptable toxicity. One study cycle equals 28 days.
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Eligibility Criteria
Age Range18 Years — N/A
SexALL
Healthy VolunteersNo
Study Sites11

Inclusion Criteria: * Male or female patients ≥ 18 years of age -WHO performance status (PS) of 0-2 -Histologically confirmed diagnosis of GIST that is unresectable or metastatic -.Available tissue specimen: • Dose-escalation part: patients must have available archival tumor tissue which can be shi...

Countries:United StatesBelgiumFranceGermanyItalyNetherlandsSpainUnited Kingdom
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