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BKM120 days 1 - 21 plus paclitaxel + carboplatin

Phase 1

Solid Tumors | Small molecule | Oncology |Novartis AG|Last Updated: Mar 31, 2017

Success Probability
Approval Probability 71%
TA Base Rate26%
Adjusted LOA41%
ML RiskLOW_RISK
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Market & Valuation
rNPV $3.2B
Market Size $9.4B
Revenue Basis $1.6B
Competitors 6
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Trial Design
CONTROLLEDDMCBiomarker
Total Trials1
Total Enrollment45
FDA Designations
No designations recorded
Clinical Trials (1)
NCT IDTitlePhaseStatusEnrollmentVelocityDesignStartCompletionLast UpdatedSitesCountries
NCT01297452BKM120 + Carboplatin + Paclitaxel for Patients With Advanced Solid TumorsPHASE1 COMPLETED 45Feb 15, 2011Mar 29, 2017Mar 31, 20171 United States
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Study Endpoints
Primary Endpoints
To establish the phase II recommended dose of daily oral BKM120
2 years

for patients with advanced solid tumors, BKM120 in combination with two different schedules of paclitaxel and carboplatin.

EXPANSION COHORT A:To evaluate the safety and tolerability of daily oral BKM120 (100 mg) + paclitaxel (200 mg/m2) + carboplatin (AUC 6), both given intravenously (IV) on day 1 of a 21-day cycle, with pegfilgrastim support
2 years
EXPANSION COHORT B: To obtain a preliminary description of efficacy of the regimen established in Group 1 among patients with tumors harboring PTEN mutation or homozygous deletion.
2 years
Secondary Endpoints
To describe the safety of BKM120 combined with paclitaxel and carboplatin,
weekly clinic visits during Cycle 1, on Day 1 of subsequent cycles,
To determine the pharmacokinetic profile of daily BKM120.
2 years
To describe and tabulate the radiographic response rate of BKM120 in combination with carboplatin and paclitaxel,
2 years
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Study Design & Arms
AllocationNON_RANDOMIZED
MaskingNONE
ModelPARALLEL
PurposeTREATMENT
Treatment Arms
ArmTypeDescription
BKM120 (days 1 - 21) + paclitaxel + carboplatinEXPERIMENTALThis will be a single institution phase I study. The primary objectives are to determine the maximum tolerated dose of BKM120 administered with paclitaxel + carboplatin on both a 21-day cycle with growth factor support (Group 1)
BKM120 (days 1 - 28, ) + paclitaxel + carboplatinEXPERIMENTALThis will be a single institution phase I study. The primary objectives are to determine the maximum tolerated dose of BKM120 administered + paclitaxel with carboplatin on a 28-day cycle with growth factor support and a 28-day cycle (Group 2).
BKM120 (days 1-21) + paclitaxel (day 1) + carboplatin (day 1)EXPERIMENTALEXPANSION COHORT A BKM120 100 mg (days 1 - 21, per dose escalation scheme) plus paclitaxel (200 mg/m2 intravenously, day 1) + carboplatin (AUC 6 intravenously, day 1) on a 21-day cycle. After enrollment to Groups 1 and 2 has been completed and all patients in Group 1 and 2 have completed the DLT monitoring period, up to 6 additional patients will be enrolled in this EXPANSION COHORT A.
BKM120 (days 1 - 21) + paclitaxel + carboplatin exp BEXPERIMENTALExpansion Cohort B will be restricted to patients with tumors known to harbor PTEN mutation or homozygous deletion. The regimen in Expansion Cohort B will be the same regimen established in Group 1 of the protocol, with BKM120 (now called buparlisib) at 100 mg/day per oral + paclitaxel (175 mg/m2) + carboplatin (AUC 5), both given intravenously (IV) on day 1 of a 21-day cycle
Interventions
NameTypeDescription
BKM120 days 1 - 21 plus paclitaxel + carboplatinDRUGPatients will receive oral daily BKM120 (days 1 - 21, per dose escalation scheme) plus paclitaxel (175 mg/m2 intravenously, day 1) + carboplatin (AUC 5 intravenously, day 1)on a 21-day cycle. Pegfilgrastim (6 mg/subcutaneously) will be administered on day 2 of each cycle.
BKM120 (days 1 - 28, ) plus paclitaxel + carboplatinDRUGPatients will receive oral daily BKM120 (days 1 - 28, per dose escalation scheme) plus paclitaxel (80 mg/m2 intravenously, days 1, 8 and 15) + carboplatin (AUC 5 intravenously, day 1) on a 28-day cycle.
BKM120 (days 1-21) + paclitaxel (day 1) + carboplatin (day 1)DRUGBKM120 100 mg (days 1 - 21, per dose escalation scheme) plus paclitaxel (200 mg/m2 intravenously, day 1) + carboplatin (AUC 6 intravenously, day 1) on a 21-day cycle. After enrollment to Groups 1 and 2 has been completed and all patients in Group 1 and 2 have completed the DLT monitoring period, up to 6 additional patients will be enrolled in this EXPANSION COHORT.A
BKM120, Paclitaxel + CarboplatinDRUGBKM120 100 mg per oral, days 1 - 21 Paclitaxel (175 mg/m2) intravenously on Day 1 Carboplatin (AUC 5) intravenously on Day 1 EXPANSION COHORT B
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Eligibility Criteria
Age Range18 Years — N/A
SexALL
Healthy VolunteersNo
Study Sites1

Inclusion Criteria: * Pathologically confirmed recurrent or metastatic advanced solid tumor, for which there is no curative-intent treatment option. Pathology confirmation must be performed at MSKCC. * Age ≥ 18 years * ECOG performance status ≤ 1 * Life expectancy of ≥ 12 weeks * Adequate bone marr...

Countries:United States
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