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BION-1301 Single Dose

Phase 3

IgA Nephropathy | Small molecule | Nephrology |Novartis AG|Last Updated: Apr 20, 2026

Success Probability
Approval Probability 71%
TA Base Rate26%
Adjusted LOA41%
ML RiskLOW_RISK
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Market & Valuation
rNPV $3.2B
Market Size $9.4B
Revenue Basis $1.6B
Competitors 6
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Trial Design
RandomizedDouble-BlindPLACEBO_CONTROLLEDDMCBiomarker
Total Trials2
Total Enrollment486
FDA Designations
No designations recorded
Clinical Trials (2)
NCT IDTitlePhaseStatusEnrollmentVelocityDesignStartCompletionLast UpdatedSitesCountries
NCT05852938A Study of Zigakibart in Adults With IgA NephropathyPHASE3 ACTIVE NOT_RECRUITING 383Jul 6, 2023Jan 25, 2028Apr 1, 2026200 United States, Argentina +21
NCT03945318Safety and Tolerability of BION-1301 in Healthy Volunteers and Adults With IgA Nephropathy (IgAN)PHASE1 ACTIVE NOT_RECRUITING 103Apr 8, 2019Apr 30, 2026Apr 20, 202616 United States, South Korea +1
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Study Endpoints
Primary Endpoints
Change from baseline in eGFR
Baseline and 104 weeks or approximately 2 years

Change from Baseline to Week 104 in eGFR using the CKD-EPI 2021 creatinine equation

Incidence of Treatment Emergent Adverse Events (TEAEs) as assessed according to the National Cancer Institute (NCI) Common Terminology Criteria for Adverse Events (CTCAE)
Participants followed from date of enrollment until the end of study, assessed up to 76 weeks.
Severity of TEAEs as assessed according to NCI-CTCAE
Participants followed from date of enrollment until the end of study, assessed up to 76 weeks.
Secondary Endpoints
Change in proteinuria (natural log UPCR)
Baseline and 40 weeks or approximately 9 months
Annualized rate of change in eGFR
104 weeks or approximately 2 years
Effect of BION-1301 on specific clinical composite endpoints (30% eGFR reduction)
Baseline and Weeks 4, 12, 24, 40, 52, 64, 76, 88, and 104
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Study Design & Arms
AllocationRANDOMIZED
MaskingDOUBLE
ModelPARALLEL
PurposeTREATMENT
Treatment Arms
ArmTypeDescription
BION-1301EXPERIMENTAL600mg subcutaneous administration every 2 weeks for 104 weeks
PlaceboPLACEBO_COMPARATORsubcutaneous administration every 2 weeks for 104 weeks
Part 1: BION-1301EXPERIMENTALUp to 5 cohorts with single ascending doses of BION-1301 administered by intravenous (IV) infusion.
Part 1: PlaceboPLACEBO_COMPARATORParticipants will receive a single dose of placebo administered by IV infusion.
Part 2: BION-1301EXPERIMENTALUp to 4 cohorts with multiple doses of BION-1301 administered by intravenous (IV) infusion.
Part 2: PlaceboPLACEBO_COMPARATORParticipants will receive placebo by IV infusion.
Part 3: BION-1301EXPERIMENTALTwo cohorts of participants will receive multiple doses of BION-1301 by IV infusion (Cohort 1) or SC injection (Cohort 2) at 600mg/biweekly.
Part 4 Retreatment: BION-1301EXPERIMENTALEligible participants from Part 3 may enroll in Part 4 due to disease progression or by choice for optional retreatment and receive SC injection at 600mg/biweekly.
Interventions
NameTypeDescription
BION-1301DRUGBION-1301 Pre-Filled Syringe (PFS) 600mg subcutaneous administration every 2 weeks for 104 weeks.
PlaceboDRUGPlacebo - PFS subcutaneous administration every 2 weeks for 104 weeks.
BION-1301 Single DoseDRUGA solution for IV infusion administered as a single dose.
Placebo Single DoseDRUGA solution by IV infusion administered as a single dose.
BION-1301 Multiple DosesDRUGA solution for IV infusion or SC injections (Part 3 only) administered as multiple doses.
Placebo Multiple DosesDRUGA solution by IV infusion administered as multiple doses.
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Eligibility Criteria
Age Range18 Years — N/A
SexALL
Healthy VolunteersNo
Study Sites200

Inclusion Criteria: * Male and female participants aged ≥ 18 years at the time of signing the informed consent form (ICF) prior to initiation of any study specific activities/procedures. * Biopsy-proven IgAN diagnosed within the past 10 years prior to Screening, that, in the opinion of the Investig...

Countries:United StatesArgentinaAustraliaBelgiumBrazilCanadaChinaCroatiaCzechiaFranceGermanyGreeceIndiaIsraelItalyJapanMalaysiaMexicoSouth KoreaSpainTaiwanTurkey (Türkiye)United Kingdom
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Recent Changes (Last 90 Days)
MEDIUMMay 26, 2026NCT03945318primaryCompletionDate: changed
MEDIUMMay 26, 2026NCT05852938primaryCompletionDate: changed
LOWMay 24, 2026NCT03945318studyFirstPostDate: changed
LOWMay 24, 2026NCT05852938studyFirstPostDate: changed