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Alvelestat - dose 1

Phase 2

Alpha 1-Antitrypsin Deficiency | Small molecule | Respiratory |Mereo BioPharma Group plc|Last Updated: Apr 13, 2022

Success Probability
Approval Probability 71%
TA Base Rate26%
Adjusted LOA41%
ML RiskLOW_RISK
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Market & Valuation
rNPV $3.2B
Market Size $9.4B
Revenue Basis $1.6B
Competitors 6
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Trial Design
UNCONTROLLED
Total Trials1
Total Enrollment99
FDA Designations
No designations recorded
Clinical Trials (1)
NCT IDTitlePhaseStatusEnrollmentVelocityDesignStartCompletionLast UpdatedSitesCountries
NCT03636347A 12-week Study Treating Participants Who Have alpha1-antitrypsin-related COPD With Alvelestat (MPH966) or Placebo.PHASE2 COMPLETED 99Oct 1, 2018Mar 1, 2022Apr 13, 2022 -
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Study Design & Arms
Interventions
NameTypeDescription
Placebo Oral TabletDRUGtwice daily administration
Alvelestat oral tablet - dose 1DRUGtwice daily administration
Alvelestat oral tablet - dose 2DRUGtwice daily administration
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