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MB07133 /m2/day

Phase 1

Hepatocellular Carcinoma | Small molecule | Oncology |Ligand Pharmaceuticals Incorporated|Last Updated: Aug 12, 2011

Success Probability
Approval Probability 71%
TA Base Rate26%
Adjusted LOA41%
ML RiskLOW_RISK
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Market & Valuation
rNPV $3.2B
Market Size $9.4B
Revenue Basis $1.6B
Competitors 6
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Trial Design
CONTROLLEDBiomarker
Total Trials1
Total Enrollment28
FDA Designations
No designations recorded
Clinical Trials (1)
NCT IDTitlePhaseStatusEnrollmentVelocityDesignStartCompletionLast UpdatedSitesCountries
NCT00073736Safety and Tolerability of I.V. Infusion of MB07133 in Patients With Unresectable Hepatocellular CarcinomaPHASE1 COMPLETED 28Sep 1, 2003 -Aug 12, 20114 United States, Hong Kong +1
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Study Endpoints
Primary Endpoints
Safety and tolerability
7-day continuous infusion every 28-days as tolerated

To determine the dose-limiting toxicities (DLT) of MB07133; To determine the maximum-tolerated continuous infusion dose (MTD) of MB07133

Secondary Endpoints
Determine effect of MB07133 on tumor size
28 day cycles
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Study Design & Arms
AllocationNON_RANDOMIZED
MaskingNONE
ModelSINGLE_GROUP
PurposeTREATMENT
Treatment Arms
ArmTypeDescription
MB07133 Dose Level 1EXPERIMENTAL7-day continuous infusion in 28-day cycles
MB07133 Dose Level 2EXPERIMENTAL7-day continuous infusion in 28-day cycles
MB07133 Dose Level 3EXPERIMENTAL7-day continuous infusion in 28-day cycles
MB07133 Dose Level 4EXPERIMENTAL7-day continuous infusion in 28-day cycles
MB07133 Dose Level 5EXPERIMENTAL7-day continuous infusion in 28-day cycles
Interventions
NameTypeDescription
MB07133 300mg/m2/dayDRUG7-day continuous infusion in 28-day cycles
MB07133 600 mg/m2/dayDRUG7-day continuous infusion in 28-day cycles
MB07133 1200 mg/m2/dayDRUG7-day continuous infusion in 28-day cycles
MB07133 1800 mg/m2/dayDRUG7-day continuous infusion in 28-day cycles
MB07133 2400 mg/m2/dayDRUG7-day continuous infusion in 28-day cycles
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Eligibility Criteria
Age Range18 Years — N/A
SexALL
Healthy VolunteersNo
Study Sites4

Inclusion Criteria: * Patients with a diagnosis of local unresectable HCC confirmed by histology using fine needle aspirate (FNA) or liver biopsy. "Local" is defined as disease either restricted to the liver or contiguous with the liver and no identifiable extrahepatic disease. * Patients with Chil...

Countries:United StatesHong KongTaiwan
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