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GWP42003 /day Dose

Phase 2

Fatty Liver | Small molecule | Metabolic |Jazz Pharmaceuticals plc|Last Updated: Aug 8, 2018

Success Probability
Approval Probability 71%
TA Base Rate26%
Adjusted LOA41%
ML RiskLOW_RISK
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Market & Valuation
rNPV $3.2B
Market Size $9.4B
Revenue Basis $1.6B
Competitors 6
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Trial Design
RandomizedDouble-BlindCONTROLLEDBiomarker
Total Trials1
Total Enrollment25
FDA Designations
No designations recorded
Clinical Trials (1)
NCT IDTitlePhaseStatusEnrollmentVelocityDesignStartCompletionLast UpdatedSitesCountries
NCT01284634Study to Evaluate the Effect of GWP42003 on Liver Fat Levels in Participants With Fatty Liver DiseasePHASE2 COMPLETED 25May 3, 2011Jul 13, 2012Aug 8, 20183 United Kingdom
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Study Endpoints
Primary Endpoints
Percent Change From Baseline To The End Of Treatment (EOT) In Mean Liver Triglyceride Levels
Baseline to EOT (Day 57) or Early Termination (ET)

Liver triglyceride levels were measured by Magnetic Resonance Imaging/Magnetic Resonance Scanning and the percent change from baseline to EOT in group mean levels was investigated. A reduction from baseline, that is, a negative value, indicates an improvement in condition.

Secondary Endpoints
Change From Baseline To The EOT In Mean Serum Total Cholesterol Levels
Baseline to EOT (Day 57) or ET
Change From Baseline To The EOT In Mean Serum High Density Lipoprotein (HDL)-Cholesterol(C) Levels
Baseline to EOT (Day 57) or ET
Change From Baseline To The EOT In Mean Serum Low-Density Lipoprotein (LDL)-C Levels
Baseline to EOT (Day 57) or ET
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Study Design & Arms
AllocationRANDOMIZED
MaskingQUADRUPLE
ModelPARALLEL
PurposeTREATMENT
Treatment Arms
ArmTypeDescription
GWP42003 200 milligrams (mg)/day DoseEXPERIMENTALParticipants self-administered one x 100 mg GWP42003 capsule twice daily for 8 weeks (the first dose was 30 minutes before breakfast \[fasted\] and the second was 30 minutes before the evening meal \[typically 12 hours apart\]).
GWP42003 400 mg/day DoseEXPERIMENTALParticipants self-administered two x 100 mg GWP42003 capsules twice daily for 8 weeks (the first dose was 30 minutes before breakfast \[fasted\] and the second was 30 minutes before the evening meal \[typically 12 hours apart\]).
GWP42003 800 mg/day DoseEXPERIMENTALParticipants self-administered four x 100 mg GWP42003 capsules twice daily for 8 weeks (the first dose was 30 minutes before breakfast \[fasted\] and the second was 30 minutes before the evening meal \[typically 12 hours apart\]).
PlaceboEXPERIMENTALParticipants self-administered one, two or four placebo capsules twice daily, for 8 weeks (the first dose was 30 minutes before breakfast \[fasted\] and the second was 30 minutes before the evening meal \[typically 12 hours apart\]). Each capsule exactly matched the GWP42003 capsules in terms of appearance, size, smell and taste.
Interventions
NameTypeDescription
GWP42003 200 mg/day DoseDRUGGWP42003 was presented as Licaps® size double zero (Size 00) hard gelatin capsules containing 100 mg of CBD dissolved in vehicle (Gelucire 44/14).
GWP42003 400 mg/day DoseDRUGGWP42003 was presented as Licaps® Size 00 hard gelatin capsules containing 100 mg of CBD dissolved in vehicle (Gelucire 44/14).
GWP42003 800 mg/day DoseDRUGGWP42003 was presented as Licaps® Size 00 hard gelatin capsules containing 100 mg of CBD dissolved in vehicle (Gelucire 44/14).
PlaceboDRUGPlacebo was presented as Licaps® Size 00 hard gelatin capsules containing excipients (Gelucire 44/14).
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Eligibility Criteria
Age Range18 Years — N/A
SexALL
Healthy VolunteersNo
Study Sites3

Inclusion Criteria: * Participant gave informed consent for participation in the study. * Participant was aged 18 years or above. * Participant had documented evidence of liver fat content ≥5% as measured by MRI/MRS scanning or a biopsy within two months prior to screening, or willing to undergo an...

Countries:United Kingdom
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