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Niraparib plus Cabozantinib

Phase 1

Urothelial Cancer | Small molecule | Oncology |GSK plc|Last Updated: Dec 31, 2024

Success Probability
Approval Probability 71%
TA Base Rate26%
Adjusted LOA41%
ML RiskLOW_RISK
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Market & Valuation
rNPV $3.2B
Market Size $9.4B
Revenue Basis $1.6B
Competitors 6
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Trial Design
UNCONTROLLEDBiomarker
Total Trials1
Total Enrollment67
FDA Designations
No designations recorded
Clinical Trials (1)
NCT IDTitlePhaseStatusEnrollmentVelocityDesignStartCompletionLast UpdatedSitesCountries
NCT03425201Niraparib in Combination with Cabozantinib (XL184) in Patients with Advanced Urothelial Cancer (NICARAGUA)PHASE1 COMPLETED 67Oct 14, 2019Jul 31, 2024Dec 31, 202410 Spain
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Study Endpoints
Primary Endpoints
Phase I: maximum tolerated dose
up to 1 month

Highest dose at which ≤1 out of 6 patients experience a DLT

Phase II: progression free survival
Up to 6 months

Time from the date of first dose of study treatment to the date of progression or death (from any cause).

Secondary Endpoints
Incidence of Treatment-Emergent Adverse Events
Up to 6 months
Phase II: Objective Response Rate
Up to 6 months
Phase II: Disease Control Rate
Up to 6 months
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Study Design & Arms
AllocationNA
MaskingNONE
ModelSINGLE_GROUP
PurposeOTHER
Treatment Arms
ArmTypeDescription
Niraparib plus CabozantinibEXPERIMENTALPatients will receive niraparib and cabozantinib p.o. once daily in 28-day cycles. In phase I, patients will be accrued to each dose level in cohorts of 6 patients. Escalation will continue until a dose-limiting toxicity (DLT) is observed or the highest dose-level is reached. In phase II study patients will receive niraparib p.o. once daily and cabozantinib p.o. once daily in 28-day cycles at doses recommended in the phase I study. If niraparib or cabozantinib need to be interrupted due to toxicity, patient can continue only with the other drug.
Interventions
NameTypeDescription
Niraparib plus CabozantinibDRUGNon-randomized trial will comprise 2 stages. A dose escalation phase will characterize the safety, tolerability, DLTs and MTD, of oral niraparib plus cabozantinib in patients with urothelial or renal cell carcinoma. Subsequently, the phase II will further evaluate the safety and antitumor activity of this combination in patients with urothelial carcinoma.
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Eligibility Criteria
Age Range18 Years — N/A
SexALL
Healthy VolunteersNo
Study Sites10

Inclusion Criteria: Phase I study: 1. Histologically confirmed UC of the urinary tract or renal cell carcinoma 2. Advanced or metastatic disease that is not amenable to curative surgery or radiation 3. Patients must be willing to provide a tumor specimen prior to enrollment 4. Previous therapy: ...

Countries:Spain
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