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zamzetoclax

Phase 1

Solid Malignancies | Small molecule | Other |Gilead Sciences, Inc.|Last Updated: Jan 7, 2026

Success Probability
Approval Probability 71%
TA Base Rate26%
Adjusted LOA41%
ML RiskLOW_RISK
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Market & Valuation
rNPV $3.2B
Market Size $9.4B
Revenue Basis $1.6B
Competitors 6
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Trial Design
CONTROLLEDBiomarker
Total Trials1
Total Enrollment145
FDA Designations
No designations recorded
Clinical Trials (1)
NCT IDTitlePhaseStatusEnrollmentVelocityDesignStartCompletionLast UpdatedSitesCountries
NCT05006794Study to Evaluate the Safety, Tolerability, and Pharmacokinetics of GS-9716 as Monotherapy and in Combination With Anticancer Therapies in Adults With Solid MalignanciesPHASE1 ACTIVE NOT_RECRUITING 145Sep 15, 2021Mar 1, 2029Jan 7, 202613 United States, Israel
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Study Endpoints
Primary Endpoints
Percentage of Patients Experiencing Dose-Limiting Toxicities (DLTs)
First dose date up to 28 days
Percentage of Patients Experiencing Adverse Events (AEs) According to National Cancer Institute (NCI) Common Terminology Criteria for AEs (CTCAE), Version 5.0
First dose date up to last dose date (Maximum: 105 weeks) plus 30 days
Secondary Endpoints
Maximum Observed Concentration (Cmax) for Zamzetoclax
Approximately 105 Weeks
Time to Maximum Observed Concentration (Tmax) for Zamzetoclax
Approximately 105 Weeks
Area Under the Concentration Versus Time Curve From Time 0 to 24 Hours (AUC0-24) for Zamzetoclax
Approximately 105 Weeks
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Study Design & Arms
AllocationNON_RANDOMIZED
MaskingNONE
ModelSEQUENTIAL
PurposeTREATMENT
Treatment Arms
ArmTypeDescription
Part A: zamzetoclax Dose-EscalationEXPERIMENTALPatients will receive escalating doses of zamzetoclax to estimate MTD.
Part A: zamzetoclax Dose-ExpansionEXPERIMENTALPatients will receive ≤ MTD of zamzetoclax.
Part B (Cohort B1): Zamzetoclax + docetaxelEXPERIMENTALPatients will receive escalating doses of zamzetoclax in combination with docetaxel.
Part B (Cohort B4): zamzetoclax + sacituzumab govitecan-hziyEXPERIMENTALPatients will receive escalating doses of zamzetoclax in combination with sacituzumab govitecan-hziy.
Part C (Cohort C1): zamzetoclax + docetaxelEXPERIMENTALPatients will receive ≤ MTD zamzetoclax in combination with docetaxel.
Part C (Cohort C4): zamzetoclax + sacituzumab govitecan-hziyEXPERIMENTALPatients will receive ≤ MTD zamzetoclax in combination with sacituzumab govitecan-hziy.
Interventions
NameTypeDescription
zamzetoclaxDRUGTablet(s) administered orally
DocetaxelDRUGAdministered intravenously
sacituzumab govitecan-hziyDRUGAdministered intravenously
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Eligibility Criteria
Age Range18 Years — N/A
SexALL
Healthy VolunteersNo
Study Sites13

Key Inclusion Criteria: General Inclusion Criteria (all cohorts): * Eastern Cooperative Oncology Group (ECOG) performance status of 0 or 1 * Measurable disease per RECIST version 1.1 * Adequate hematology, renal and hepatic function * Left ventricular ejection fraction (LVEF) ≥ 50% * Patients with...

Countries:United StatesIsrael
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Recent Changes (Last 90 Days)
LOWMay 26, 2026NCT05006794primaryCompletionDate: changed
LOWMay 24, 2026NCT05006794studyFirstPostDate: changed