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Tirabrutinib

Phase 1

Primary Central Nervous System Lymphoma (PCNSL) | Small molecule | Oncology |Co-Diagnostics, Inc.|Last Updated: Apr 16, 2026

Success Probability
Approval Probability 71%
TA Base Rate26%
Adjusted LOA41%
ML RiskLOW_RISK
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Market & Valuation
rNPV $3.2B
Market Size $9.4B
Revenue Basis $1.6B
Competitors 6
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Trial Design
CONTROLLEDBiomarker
Total Trials1
Total Enrollment40
FDA Designations
No designations recorded
Clinical Trials (1)
NCT IDTitlePhaseStatusEnrollmentVelocityDesignStartCompletionLast UpdatedSitesCountries
NCT07198087A Study to Investigate the Pharmacokinetics of Tirabrutinib in Participants With Mild, Moderate, and Severe Hepatic Impairment Compared to Healthy ParticipantsPHASE1 ACTIVE NOT_RECRUITING 40Oct 1, 2025Dec 31, 2026Apr 16, 20263 United States
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Study Endpoints
Primary Endpoints
Pharmacokinetic parameter of tirabrutinib: Cmax
72 hour
Pharmacokinetic parameter of tirabrutinib: Tmax
72 hour
Pharmacokinetic parameter of tirabrutinib: AUClast
72 hour
Pharmacokinetic parameter of tirabrutinib: AUCinf
72 hour
Pharmacokinetic parameter of tirabrutinib: T1/2
72 hour
Pharmacokinetic parameter of tirabrutinib: CL/F
72 hour
Pharmacokinetic parameter of tirabrutinib: Volume of distribution (Vd)
72 hour
Protein binding ratio of tirabrutinib in plasma
72 hour
Secondary Endpoints
Safety and tolerability: Vital signs (pulse rate)
72 hour
Safety and tolerability: Vital signs (blood pressure)
72 hour
Safety and tolerability: Vital signs (respiratory rate)
72 hour
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Study Design & Arms
AllocationNON_RANDOMIZED
MaskingNONE
ModelPARALLEL
PurposeOTHER
Treatment Arms
ArmTypeDescription
Tirabrutinib (Mild Hepatic Impairment)EXPERIMENTALParticipants received a single dose of Tirabrutinib 80 mg administered orally on Day 1.
Tirabrutinib (Moderate Hepatic Impairment)EXPERIMENTALParticipants received a single dose of Tirabrutinib 80 mg administered orally on Day 1.
Tirabrutinib (Severe Hepatic Impairment)EXPERIMENTALParticipants received a single dose of Tirabrutinib 80 mg administered orally on Day 1.
Tirabrutinib (Normal Hepatic Function)EXPERIMENTALParticipants received a single dose of Tirabrutinib 80 mg administered orally on Day 1.
Interventions
NameTypeDescription
TirabrutinibDRUGAdministered orally
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Eligibility Criteria
Age Range18 Years — 75 Years
SexALL
Healthy VolunteersYes
Study Sites3

Inclusion Criteria: * Male or female participants, age 18 to 75, inclusive, at the time of informed consent. * BMI between 18 and 40 kg/m2, inclusive, at Screening. * Continuous non-smokers or smokers who smoke 20 cigarettes or fewer per day. * Willingness and ability to swallow study intervention ...

Countries:United States
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