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Jaktinib

Phase 3

Myelofibrosis | Small molecule | Other |Co-Diagnostics, Inc.|Last Updated: Nov 13, 2023

Success Probability
Approval Probability 71%
TA Base Rate26%
Adjusted LOA41%
ML RiskLOW_RISK
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Market & Valuation
rNPV $3.2B
Market Size $9.4B
Revenue Basis $1.6B
Competitors 6
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Trial Design
RandomizedDouble-BlindACTIVE_CONTROLLEDBiomarker
Total Trials1
Total Enrollment105
FDA Designations
No designations recorded
Clinical Trials (1)
NCT IDTitlePhaseStatusEnrollmentVelocityDesignStartCompletionLast UpdatedSitesCountries
NCT04617028Jaktinib Versus Hydroxycarbamide in Subjects With Intermediate-2 or High-risk MyelofibrosisPHASE3 COMPLETED 105Feb 5, 2021Oct 18, 2023Nov 13, 20231 China
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Study Endpoints
Primary Endpoints
Splenic response rate at Week 24
Week 24

Splenic response rate at Week 24 is defined as the proportion of participants achieving a ≥ 35% reduction in spleen volume at Week 24 from baseline as measured by MRI or CT

Secondary Endpoints
Proportion of transfusion dependent patients converted to non-transfusion dependent patients at baseline
From start of drug administration up to 7 days after last dose of study treatment
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Study Design & Arms
AllocationRANDOMIZED
MaskingDOUBLE
ModelPARALLEL
PurposeTREATMENT
Treatment Arms
ArmTypeDescription
JaktinibEXPERIMENTALParticipants will receive Jaktinib plus placebo to match Hydroxycarbamide.
HydroxycarbamideACTIVE_COMPARATORParticipants will receive Hydroxycarbamide plus placebo to match Jaktinib.
Interventions
NameTypeDescription
JaktinibDRUGJaktinib Hydrochloride Tablets administered orally twice daily
Placebo to match HydroxycarbamideDRUGPlacebo to match Hydroxycarbamide Tablets administered orally twice daily
Hydroxycarbamide TabletsDRUGHydroxycarbamide Tablets administered orally twice daily
Placebo to match JaktinibDRUGPlacebo to match Jaktinib Tablets administered orally twice daily
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Eligibility Criteria
Age Range18 Years — 75 Years
SexALL
Healthy VolunteersNo
Study Sites1

Inclusion Criteria: * Age ≥ 18 years old,either male or female; * Subjects diagnosed with a PMF according to World Health Organiztion criteria (2016 Edition), or patients diagnosed with a Post-PV-MF or Post-EF-MF according to International Working Group for Myeloproliferative Neoplasms Research and...

Countries:China
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