Recent Updates
Recently added Catalysts

Denosumab /ML

Phase 2

Langerhans Cell Histiocytosis | Small molecule | Other |Bone Biologics Corp|Last Updated: Jan 15, 2025

Success Probability
Approval Probability 71%
TA Base Rate26%
Adjusted LOA41%
ML RiskLOW_RISK
Premium
Market & Valuation
rNPV $3.2B
Market Size $9.4B
Revenue Basis $1.6B
Competitors 6
Premium
Trial Design
UNCONTROLLEDBiomarker
Total Trials1
Total Enrollment10
FDA Designations
No designations recorded
Clinical Trials (1)
NCT IDTitlePhaseStatusEnrollmentVelocityDesignStartCompletionLast UpdatedSitesCountries
NCT03270020Denosumab for the Treatment of Adult LCHPHASE2 COMPLETED 10Sep 7, 2017Jan 14, 2025Jan 15, 20251 Greece
Unlock Drug Trial Details
Study Endpoints
Primary Endpoints
Primary efficacy endpoint: effect of denosumab treatment on the activity status of the disease (Incidence of patients with active disease)
8 months

The primary efficacy endpoint will be measured through the incidence of patients with active disease at Month 8. Given that all patients have active disease at baseline the incidence of patients with active disease at Month 8 will provide the efficacy of denosumab in controlling the disease within this time frame.

Secondary Endpoints
Secondary efficacy endpoint: development of disease-related permanent sequelae during the study period (Incidence of disease-related permanent sequelae)
18 months
Unlock Study Endpoints
Study Design & Arms
AllocationNA
MaskingNONE
ModelSINGLE_GROUP
PurposeTREATMENT
Treatment Arms
ArmTypeDescription
Treatment armEXPERIMENTALThis is a single arm study; the study arm include all patients participating in the study who will all receive Denosumab 70 MG/ML \[Xgeva\]
Interventions
NameTypeDescription
Denosumab 70 MG/ML [Xgeva]DRUGAs already described in arm description
Unlock Study Design Details
Eligibility Criteria
Age Range18 Years — N/A
SexALL
Healthy VolunteersNo
Study Sites1

Inclusion Criteria: * Adults (\>18 years of age) * Definitive diagnosis of LCH \[Based on clinic-pathological evidence with microscopic examination and at least one of the following immunological staining: Langerin (CD 207) positivity, Cluster of Differentiation 1a (CD1a) positivity, Presence of Bi...

Countries:Greece
Unlock Eligibility Criteria