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budesonode + terbutaline 'as needed'

Phase 3

Asthma | Small molecule | Respiratory |AstraZeneca PLC|Last Updated: Nov 25, 2019

Success Probability
Approval Probability 71%
TA Base Rate26%
Adjusted LOA41%
ML RiskLOW_RISK
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Market & Valuation
rNPV $3.2B
Market Size $9.4B
Revenue Basis $1.6B
Competitors 6
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Trial Design
RandomizedDouble-BlindACTIVE_CONTROLLED
Total Trials1
Total Enrollment4,215
FDA Designations
No designations recorded
Clinical Trials (1)
NCT IDTitlePhaseStatusEnrollmentVelocityDesignStartCompletionLast UpdatedSitesCountries
NCT02224157A Clinical Study to Evaluate Symbicort Turbuhaler Used 'as Needed' in Adults and Adolescents With AsthmaPHASE3 COMPLETED 4,215Nov 28, 2014Aug 16, 2017Nov 25, 2019340 Australia, Brazil +23
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Study Endpoints
Primary Endpoints
Annual Severe Asthma Exacerbation Rate - Non-inferiority Analysis
up to 52 weeks

Severe asthma exacerbations over the randomised treatment period, negative binomial model for non-inferiority test evaluation

Annual Severe Asthma Exacerbation Rate - Superiority Analysis
up to 52 weeks

Severe asthma exacerbations over the randomised treatment period, negative binomial model for superiority test evaluation

Secondary Endpoints
Number of Participants Experiencing at Least One Severe Asthma Exacerbation
Day 1 up to 52 weeks
Average Change From Baseline in Pre-bronchodilator FEV1
Study weeks 0,17, 34, 52
Number of Participants With Study Specific Asthma Related Discontinuation
Day 1 up to 52 weeks
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Study Design & Arms
AllocationRANDOMIZED
MaskingTRIPLE
ModelPARALLEL
PurposeTREATMENT
Treatment Arms
ArmTypeDescription
Symbicort "as needed"+placebo Pulmicort bidEXPERIMENTALSymbicort (budesonide/formoterol) Turbuhaler 160/4.5 μg 'as needed' + Placebo Pulmicort Turbuhaler 200 μg bid
Pulmicort bid + terbutaline "as needed"ACTIVE_COMPARATORPulmicort 200 μg Turbuhaler bid + terbutaline 0.4 mg Turbuhaler 'as needed'
Interventions
NameTypeDescription
budesonide/formoterol 'as needed' + budesonide placebo bidDRUGSymbicort (budesonide/ formoterol) 160/4.5 μg powder for inhalation 'as needed' plus Pulmicort placebo 200 μg powder for inhalation, 1 inhalation twice daily (morning and evening), 52-week treatment
budesonode bid + terbutaline 'as needed'DRUGPulmicort (budesonide) 200 μg powder for inhalation, 1 inhalation twice daily (morning and evening) plus terbutaline 0.4 mg powder for inhalation 'as needed', 52-week treatment
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Eligibility Criteria
Age Range12 Years — 130 Years
SexALL
Healthy VolunteersNo
Study Sites340

Inclusion Criteria: 1. Provision of informed consent prior to any study specific procedures. For patients under-age, signed informed consent from both the patient and the patient's parent/legal guardian is required 2. Male or Female, ≥12 years of age 3. Documented diagnosis of asthma for at least 6...

Countries:AustraliaBrazilBulgariaChileColombiaCzechiaFranceGermanyHungaryMexicoNew ZealandPeruPhilippinesPolandRomaniaRussiaSaudi ArabiaSlovakiaSouth AfricaSouth KoreaSpainSwedenThailandUkraineVietnam
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